Gaucher Disease Outcome Survey (GOS)

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Gaucher Disease Outcome Survey (GOS)

Brief description of study

The Gaucher Outcome Survey (GOS) is a long term observational survey. This survey aims to collect as much information as possible from as many Gaucher disease patients about the course of their disease, their medical management & the use of current or past medications or treatments, if any. Patient participation in GOS will be voluntary & GOS will be open to patients with Gaucher disease of any phenotype. Patients who are naïve to treatment, patients who are currently or have been previously treated with VPRIV, as well as patients who have been exposed to or are currently receiving other treatments for Gaucher disease may be included. This study is designed to gain a better understanding of the clinical course of the disease and its response to VPRIV therapy, thereby improving the clinical management of patients affected by Gaucher disease.

Clinical Study Identifier: 11-01170

ClinicalTrials.gov Identifier: NCT03291223

Principal Investigator: Nicolas Julian Abreu.

Other Investigator: Berrin Monteleone.

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