A Phase 1/2a Study to Evaluate the Safety Tolerability Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION717 in Patients with Prion Disease

Brief description of study

The purpose of this research study is to evaluate whether ION717 is safe, well-tolerated, and determine how it affects and processes in the human body.


Clinical Study Identifier: s23-00627
ClinicalTrials.gov Identifier: NCT06153966


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