Randomized Double-Blind Placebo-controlled Safety Study of Glial Cell Line-Derived Neurotrophic Factor Gene Transfer (AAV2-GDNF) in Multiple System Atrophy

Brief description of study

In this clinical trial, we are testing a drug called glial cell line-derived neurotrophic factor (GDNF) gene transfer to see if it helps people with Multiple System Atrophy (MSA). GDNF gene is delivered to a part of the brain involved in MSA. This study will evaluate the safety of this study drug, and see whether it can improve the course of MSA.


Clinical Study Identifier: s23-01175
ClinicalTrials.gov Identifier: NCT04680065


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