Mucopolysaccharidosis Type VII Disease Monitoring Program (MPS VII DMP)

Brief description of study

You are being asked if you want to join this study because you have Mucopolysaccharidosis Type VII (“MPS 7”,“MPS VII”, or “Sly Syndrome”). The purpose of this study is to help us understand the disease that you have been diagnosed with called “MPS 7”,“MPS VII”, or “Sly syndrome” and the effect of the treatment of vestroidase alfav(formally called UX003) if you are receiving it. You may have received this treatment in the past.


Clinical Study Identifier: s17-01533
Principal Investigator: Heather Ann Lau.


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