Displaying 52 (all) recruiting clinical trials.
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DISCOVERY of Risk Factors for Type 2 Diabetes in Youth Study
Type 2 Diabetes (T2D) is a medical condition in which high blood sugars develop in the body. The DISCOVERY study team is doing this study ...Phase N/A
Non-Interventional
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Site for Intermediate Patient Population Expanded Access Protocol for MBP134 for Participants with Sudan Virus Disease (SVD)
The goal of this study is to see if a drug called MBP134 works to help patients get better from Sudan Virus Disease (SVD).Phase N/A
Interventional
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A Prospective Observational Sub-Study of the Global Hypophosphatasia Registry to Describe the Potential Risk of Immune-Mediated Loss of Pharmacological Effect of Asfotase Alfa in Participants with Hypophosphatasia (HPP)
This study collects observational Standard of Care (SOC) data in patients currently receiving asfotase alfa or about to start treatment with asfotase alfa as determined ...Phase N/A Non-Interventional
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The Prospective Natural History of Congenital Insensitivity to Pain with the Anhidrosis (CIPA)
The purpose of this study is to create a database of clinical information collected from you/your child’s medical chart on a yearly basis ...Phase N/A Non-Interventional
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Understanding Disease Burden in Biliary Atresia
It is our understanding that Biliary atresia (BA) can significantly affect a BA patient’s quality of life.? This study aims to assess the frequency ...Phase N/A Non-Interventional
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Collaborative Registry to Determine the Natural History of Barth Syndrome
The purpose of this research study is to collect data that we hope will help answer those questions and improve outcomes for children with Barth ...Phase N/A Non-Interventional
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SINGLE-CENTER OBSERVATIONAL STUDY OF SEIZURE TYPES IN RARE GENETIC EPILEPSIES
The purpose of this research study is to better describe specific movements that are seizures in rare genetic epilepsies (which may be different than other ...Phase N/A Non-Interventional
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FMT and Other Gut Microbial Therapies National Registry
A national data registry of patients receiving fecal microbiota transplantation (FMT) or other gut-related-microbiota products designed to prospectively assess short and long-term safety and effectiveness.Phase N/A Non-Interventional
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A single-center observational study of whole and regional brain volumes in patients with pediatric-onset demyelinating diseases
The purpose of this research study is to better understand how the brains of children and young adults with demyelinating diseases, such as multiple sclerosis ...Phase N/A Non-Interventional
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Prospective Registry-Based Study Evaluating the Effectiveness and Safety of Odevixibat in Participants with Alagille Syndrome (ALGS)
The purpose of this research study is to gather information on how well Bylvay (Odevixibat) works for treating Alagille syndrome using real-life data collected over ...Phase N/A Non-Interventional
