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HEAD START 4: NEWLY DIAGNOSED CHILDREN (LESS THAN 10 YEARS OLD) WITH MEDULLOBLASTOMA AND OTHER CENTRAL NERVOUS SYSTEM EMBRYONAL TUMORS
If your child has been diagnosed with medulloblastoma or other central nervous system embryonal tumors, your child may qualify to participate in a study. The ...
Phase
Interventional
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Correlation of clinical response of children with short stature to growth hormone therapy and composition of the gut microbiome.
There are normally bacteria present in everyone's gut. The purpose of this study is to evaluate if the subjects with short stature have different ...Phase N/A
Non-Interventional
Accepts Healthy Volunteer
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NN8640-4245 - A dose-finding trial evaluating the effect and safety of once-weekly treatment of somapacitan compared to daily Norditropin in children with short stature born small for gestational age with no catch-up growth by 2 years of age or older
This research study involves children born small and who stayed small. Treatment is somapacitan once a week compared to Norditropin® once a day. Researchers will ...Phase
Interventional
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A trial comparing the effect and safety of once weekly dosing of somapacitan with daily Norditropin in children with growth hormone deficiency
Purpose of the research study is to collect information to help us understand how doctors treat and manage children and adolescent with growth hormone deficiency ...Phase
Interventional
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Neonatal saliva and urine exosomes as non-invasive biomarkers for neonatal outcomes in preterm infants
The purpose of this study is to evaluate if biomarkers measured in body fluids (such as saliva, urine, and blood) and stool samples are associated ...Phase N/A Non-Interventional
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Cold milk as a novel therapy for dysphagia in preterm infants
This is a research study to evaluate if drinking cold milk (breast milk or formula at 4-9°C Temp) improves swallowing in premature babies who ...Phase N/A Interventional
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Gut Microbiome in Food Protein-Induced Enterocolitis Syndrome: An Observational Study
Food protein-induced enterocolitis syndrome (FPIES) is a non IgE-mediated gastrointestinal food allergy that causes severe, projectile, repetitive vomiting in infants and may cause dehydration and ...Phase N/A Non-Interventional
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A PHASE 3 OPEN-LABEL RANDOMIZED MULTICENTER 12 MONTHS EFFICACY AND SAFETY STUDY OF WEEKLY MOD-4023 COMPARED TO DAILY GENOTROPIN THERAPY IN PRE-PUBERTAL CHILDREN WITH GROWTH HORMONE DEFICIENCY
The purpose of this study is to compare the effectiveness, safety and handling of the investigational drug MOD-4023 (weekly injections, initial dose of 0.66 ...Phase
Interventional
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Organized sports participation among patients who have undergone Ponseti treatment for Idiopathic Clubfoot
The purpose of this study is to evaluate the regularity of sports participation in children, with a diagnosis of clubfoot, at the grade school, middle ...Phase N/A Non-Interventional
Accepts Healthy Volunteer
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A phase 2 open-label single-arm cohort study to evaluate the safety efficacy and pharmacokinetics of sparsentan treatment in pediatric subjects with selected proteinuric glomerular diseases (EPPIK)
The purpose of this research study is to study if an investigational drug (one that is not FDA approved), named sparsentan, will help in the ...Phase
Interventional
