Displaying 86 (all) recruiting clinical trials.
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Tuberous Sclerosis Complex Biosample Repository and Natural History Database Project
The purpose of the project is to learn more about tuberous sclerosis complex (TSC) which may lead to new treatments for conditions that affect different ... -
MACI Patient Registry and Data Repository
The objective of the Matrix-induced autologous chondrocyte implantation (MACI) Registry is to allow the collection of demographic, treatment, and outcome data at sites in the ... -
A Global Prospective Observational Registry of Patients with Pompe Disease
The purpose of this registry is to evaluate clinical outcomes in participants with Pompe disease. This includes what happens to participants who are not on ... -
DISCOVERY of Risk Factors for Type 2 Diabetes in Youth Study
Type 2 Diabetes (T2D) is a medical condition in which high blood sugars develop in the body. The DISCOVERY study team is doing this study ... -
A Phase 1/2 Study to Evaluate the Safety and Efficacy of AZD0486 in Adolescent and Adult Participants with Relapsed or Refractory B-Cell Acute Lymphoblastic Leukaemia
This study is designed to test how effective a new drug called AZD0486 (BITE for CD19) is for patients relapsed/refractory B-cell acute lymphoblastic leukemia ...
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Site for Intermediate Patient Population Expanded Access Protocol for MBP134 for Participants with Sudan Virus Disease (SVD)
The goal of this study is to see if a drug called MBP134 works to help patients get better from Sudan Virus Disease (SVD). -
The Prospective Natural History of Congenital Insensitivity to Pain with the Anhidrosis (CIPA)
The purpose of this study is to create a database of clinical information collected from you/your child’s medical chart on a yearly basis ... -
Collaborative Registry to Determine the Natural History of Barth Syndrome
The purpose of this research study is to collect data that we hope will help answer those questions and improve outcomes for children with Barth ... -
<strong>Adolescents:</strong> A Prospective Single Arm Open Label Trial to Confirm Safety and Effectiveness of Prism as an Adjunct to Standard of Care in Adolescents with Post-Traumatic Stress Disorder (PTSD)
The purpose of this research study is to is to establish if the FDA-approved Prism device, currently used for treating adult PTSD patients can also ... -
Immunologic Basis of Food Protein-Induced Enterocolitis Syndrome (INFINITY)
The purpose of this study is to find out if a new low-dose oral food challenge (OFC) over 7 days can accurately diagnose food protein-induced ...