Displaying 79 (all) recruiting clinical trials.
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A Phase 2/3 Multicenter Randomized Double-Blind Placebo-Controlled Study to Evaluate the Efficacy Safety and Tolerability of BHV-7000 in Subjects with Refractory Focal Epilepsy
The main purpose of this study is to understand whether BHV-7000 can help reduce the number of seizures in subjects with difficult to control or ...Phase
Interventional
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DISCOVERY of Risk Factors for Type 2 Diabetes in Youth Study
Type 2 Diabetes (T2D) is a medical condition in which high blood sugars develop in the body. The DISCOVERY study team is doing this study ...Phase N/A
Non-Interventional
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A Phase 1/2 Study to Evaluate the Safety and Efficacy of AZD0486 in Adolescent and Adult Participants with Relapsed or Refractory B-Cell Acute Lymphoblastic Leukaemia
This study is designed to test how effective a new drug called AZD0486 (BITE for CD19) is for patients relapsed/refractory B-cell acute lymphoblastic leukemia ...
Phase
Interventional
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Site for Intermediate Patient Population Expanded Access Protocol for MBP134 for Participants with Sudan Virus Disease (SVD)
The goal of this study is to see if a drug called MBP134 works to help patients get better from Sudan Virus Disease (SVD).Phase N/A Interventional
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A Prospective Observational Sub-Study of the Global Hypophosphatasia Registry to Describe the Potential Risk of Immune-Mediated Loss of Pharmacological Effect of Asfotase Alfa in Participants with Hypophosphatasia (HPP)
This study collects observational Standard of Care (SOC) data in patients currently receiving asfotase alfa or about to start treatment with asfotase alfa as determined ...Phase N/A Non-Interventional
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The Prospective Natural History of Congenital Insensitivity to Pain with the Anhidrosis (CIPA)
The purpose of this study is to create a database of clinical information collected from you/your child’s medical chart on a yearly basis ...Phase N/A Non-Interventional
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Understanding Disease Burden in Biliary Atresia
It is our understanding that Biliary atresia (BA) can significantly affect a BA patient’s quality of life.? This study aims to assess the frequency ...Phase N/A Non-Interventional
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Collaborative Registry to Determine the Natural History of Barth Syndrome
The purpose of this research study is to collect data that we hope will help answer those questions and improve outcomes for children with Barth ...Phase N/A Non-Interventional
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A Platform Study of RAS(ON) Inhibitor Combinations in Patients with RAS-Mutated Non-Small Cell Lung Cancer (NSCLC)
This study is designed to test how effective a new drug called AZD0486 (BITE for CD19) is for patients relapsed/refractory B-cell acute lymphoblastic leukemia ...
Phase
Interventional
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Randomized Double-Blind Placebo-Controlled Phase 3 Study to Evaluate the Efficacy and Safety of Maralixibat in the Treatment of Participants with Cholestatic Pruritus (EXPAND)
The purpose of this clinical research study is to learn more about the use of the study drug, maralixibat, for the treatment of cholestatic pruritus ...Phase
Interventional
